Vidéo
Little Issue: Young Minds Matter
🌟 𝗬𝗼𝘂𝗻𝗴 𝗠𝗶𝗻𝗱𝘀 𝗠𝗮𝘁𝘁𝗲𝗿: Discover how Little Issue…
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Learn about rare diseases, science and history through our podcasts, webinars and videos.
Vidéo
Rare Care: how new medicines are made
🔬 Developing and funding treatments for rare diseases present distinct challenges that traditional funding models often can’t address. With small patient populations, high research costs, and limited commercial incentives, innovation for rare disease requires new approaches. 🙌 Filmed at UC San Diego during the…
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Vidéo
Behind the scene of “Je suis autiste… et alors?”
📚 Go behind the scenes of the book “I’m Autistic… So What?” 👉A powerful and uplifting testimony about autism, available for free in both digital and print versions. 🎙️ At just 26 years old, Maxime Vindrier has established himself as a vital voice in autism awareness. Diagnosed at age…
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Vidéo
A Conversation with Teri Wiley, Managing Director at Pathways to Cures
At LaunchBio’s Invest in Cures Event in San Diego, Teri Wiley, Partners, Managing Director at Pathways to Cures shared important insights on venture philanthropy in the context of bleeding disorders. …
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Vidéo
Understanding gene therapy for rare diseases
During our conversation with Dr. Stephanie Cherqui at the Invest in Cures event by LaunchBio, we explored the transformative impact of gene therapy in treating genetic disorders, especially rare diseases. Meet Dr. Stephanie Cherqui Dr. Cherqui is a professor at the University of…
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Webinar
Keys to success: Unlocking health care access for rare disease
This webinar aims to share insights, experiences, and best practices in navigating the complexities of health care systems to ensure equitable access for rare disease patients
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Webinar
Standing out in the storm: Caregiving in rare disease
This webinar aims to provide caregivers with valuable knowledge and strategies to navigate the complexities of caregiving in the context of rare diseases.
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Webinar
Blooming against odds: Successfully navigating mental health in rare disease
The discussion aims to empower individuals with rare diseases to not only survive but thrive in their journey towards mental health and well-being.
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Webinar
Advocacy in rare disease: Taking Care of Caregivers
In this panel discussion, participants will explore advocacy efforts aimed at easing the burden of caregiving for rare diseases.
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Webinar
Advocacy in rare disease: Driving Technology Advances
In this panel discussion, participants will discuss how technology advancements could bring new therapies.
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Webinar
Advocacy in rare disease: Working the Regulatory Angle
In this panel discussion, participants will discuss how to navigate the notoriously complex regulatory angle
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Webinar
Advocacy in rare disease: Closing the funding gap
In this panel discussion, participants will discuss how closing the funding gap in rare diseases requires a multi-faceted approach.
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