Novel therapeutics

A new hope for curing Amyotrophic lateral sclerosis

Dr. Maria Grazia Biferi (Centre of Research in Myology (CRM), Paris) and her team successfully designed, conceived and optimized a gene therapy protocol for ALS (Amyotrophic Lateral Sclerosis).

How to regenerate injured spinal cord?

Researchers are working to understand why the nerves of the central nervous system fail to repair themselves, in the hope of finding ways to reboot the regeneration process.

Gene editing restores dystrophin expression in a canine model of Duchenne muscular dystrophy

Eric Olson's team used AAV gene therapy vectors to deliver CRISPR gene editing components in a larger animal model of Duchenne Muscular Dystrophy

The revolution of Immunotherapy

Immunotherapy is the most relevant breakthrough in cancer therapy. Discover this revolution